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Golodirsen

Composition

This Formulation contains Golodirsen as a active pharmaceutical ingrediant

Indications

Golodirsen is indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients with a confirmed mutation amenable to exon 53 skipping.

Side effects

Common side effects include headache, pyrexia (fever), cough, vomiting

Precautions

cautiosly used in patients having renal impairment.

Contraindications

Contraindicated in patients those who have serious hypersensitivity towards Golodirsen

Dosage and administration

30 mg once in a week through IV infusion

Countries

Unites states

Available Forms

Solution for IV infusion